Oral Presentation Matrix Biology Society of Australia and New Zealand Annual Meeting 2012

DISCOVERY OF PG545: A HIGHLY POTENT AND SIMULTANEOUS INHIBITOR OF ANGIOGENESIS, TUMOR GROWTH AND METASTASIS (#12)

Vito Ferro 1
  1. School of Chemistry & Molecular Biosciences, University of Queensland, Brisbane, Queensland, Australia

Increasing the aglycone lipophilicity of a series of polysulfated oligosaccharide glycoside heparan sulfate (HS) mimetics1 via attachment of a steroid or long chain alkyl group resulted in compounds with significantly improved in vitro and ex vivo antiangiogenic activity.  The compounds potently inhibited heparanase and HS-binding angiogenic growth factors, and displayed improved antitumor and antimetastatic activity in vivo compared with the earlier series. Preliminary pharmacokinetic analyses also revealed significant increases in half-life following i.v. dosing, ultimately supporting less frequent dosing regimens in preclinical tumor models2 compared with other HS mimetics. The compounds also displayed only mild anticoagulant activity, a common side effect usually associated with HS mimetics.  These efforts led to the identification of PG545 as a clinical candidate.3   PG545 is currently under evaluation in Phase I clinical trials in cancer patients.  

  1. Johnstone, K. D.; Karoli, T.; Liu, L.; Dredge, K.; et al. J. Med. Chem. 2010, 53, 1686.
  2. Dredge, K.; Hammond, E.; Handley, P.; Gonda, T. J.; et al. Br. J. Cancer 2011, 104, 635.
  3. Ferro, V.; Liu, L.; Johnstone, K. D.; Wimmer, N.; et al. J. Med. Chem. 2012, 55, 3804.